Two Children Die After Receiving Novartis Gene Therapy
No deaths had previously been associated with the muscle-wasting treatment Zolgensma. ABOVE:© ISTOCK.COM, HOHL The drug company Novartis reported yesterday (August 11) that two children suffering from spinal muscular atrophy—a rare, frequently fatal muscle-wasting disease—died of acute liver failure within five to six weeks of taking the gene therapy Zolgensma, several outlets report. Novartis has notified […]
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Scientists Identify Neurons Needed to Walk After Paralysis
Nine people with spinal injuries walked again after electrical stimulation, allowing researchers to pinpoint neurons likely underlying their recovery. Amanda Heidt Nov 10, 2022 | 3 min readPDF VERSION ABOVE:Visualization of the neurons involved in regaining the ability to walk after paralysisNEURORESTORE/JIMMY RAVIER Scientists now have a better understanding of how our bodies respond to spinal […]
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New Gene Mutants Identified in Rare Motor Neuron Diseases
The discovery of gene variants in cases of hereditary spastic dysplasia could provide a diagnosis to affected families where no genetic cause could be found before. EDITOR’S CHOICE IN CELL BIOLOGY Geneticists Emma Baple and Andrew Crosby previously discovered mutations in more than 15 genes that cause hereditary spastic paraplegia (HSP)—a group of rare inherited disorders characterized by leg […]
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